Current Appeal

Funding preclinical studies

Developing clinical trial plans

 

 

Planning for clinical trials to test the effectiveness in HSPers of drugs that have proved successful with HSP stem cells in the laboratory commenced in late 2016 and is continuing.

 

Over 2017 and 2018, two dose modelling studies have been carried out – a computer-based modelling initially, followed by a study in mice.

 

While planning is not sufficiently developed to allow costing and budgeting estimates to be developed, we already know that it will take all the money we have plus quite a bit more to implement the clinical trials. Funding of the overall process through government, institutional and philanthropic grants, private equity investors and commercial partnership with a pharmaceutical company has also been discussed and now requires concerted investigation and consideration to ensure the best decisions are made over time in the interests of establishing an effective treatment that is widely available and affordable to HSPers globally.

 

Your generous and continuing support helps make this possible. 99 cents in every dollar you give goes directly to fund the HSP research program. Gifts of $2 or more are tax-deductible.

An effective treatment for HSP is now within reach