His inspiration yielding results
Foundation News
28 February is Rare Disease Day
Show your support
NDIS funding cuts
Tens of thousands affected
Groundbreaking UN Resolution on Rare Diseases
Adopted by all 193 Member States
New Foundation collaboration
Genetic Cures for Kids
US HSP support group
Latest newsletter
Research program update December 2021
Research team members presenting
International Day of People with Disability
Friday, 3 December, 2021
Accelerating gene therapies for rare diseases
$76 million over 5 years to be invested
Rescuing drug castoffs
Finding a development path for promising drugs