Research Highlights

Biomarker matches drug levels in mouse brain tissue

May assist outcome measures in clinical trials

Imaging-based method a potential biomarker

Biochemical studies shed light on disease mechanism

Disease-causing mechanisms described

Multi-faceted studies the key

Key enzyme in muscle health and degeneration

Research from Iran, Germany, Canada, Sweden, Sudan, France, China, South Korea, India

Evidence established in large study

Speech therapy evaluation recommended